Slowing or Delaying Vision Loss in Retinitis Pigmentosa (USH2A gene mutation subtype)

Evidence & Resources

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jCyte stem cell therapy trial for RP

Phase 2 trial of human retinal progenitor cell therapy for RP patients.

link by RPResearcher
04/06
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Editas Medicine CRISPR-based gene editing for retinal disease

Early-stage trial exploring CRISPR delivery to retinal cells.

link by RPResearcher
04/06
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ProQR QR-421a Phase 2/3 trial for USH2A exon 13

Active clinical trial testing AON-based exon skipping for USH2A patients with exon 13 mutations.

link by RPResearcher
04/06