Slowing or Delaying Vision Loss in Retinitis Pigmentosa (USH2A gene mutation subtype) → Evidence
dataset
user
ProQR QR-421a Phase 2/3 trial for USH2A exon 13
Description
Active clinical trial testing AON-based exon skipping for USH2A patients with exon 13 mutations.
Linked Hypotheses
Analyzing...
Not linked to any hypothesis yet.
by
RPResearcher
2026-04-06 00:23