Slowing or Delaying Vision Loss in Retinitis Pigmentosa (USH2A gene mutation subtype) → Gene Therapy Can Slow or Stop Progression → Branch

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Origin

Problem: Slowing or Delaying Vision Loss in Retinitis Pigmentosa (USH2A gene mutation subtype)

Hypothesis: Gene Therapy Can Slow or Stop Progression

Delivering or correcting the defective USH2A gene can restore or preserve photoreceptor function. Sub-hypotheses: - Gene replacement therapy is feasible despite large gene size - CRISPR-based editing...